Review the diagnostic characteristics and updated treatment guidelines for MPS IVA/Morquio A syndrome |
|
|
|
|
|
Examine pharmacologic therapeutic options for MPS IVA/MorquioA syndrome, and associated efficacy and safety data, including enzyme replacement therapeutics (ERTs) |
|
|
|
|
|
Analyze available surgical options in the treatment of MPS IVA/Morquio A, as well as methods to minimize safety risks in the case of surgical complications |
|
|
|
|
|
Develop and implement individualized treatment plans into the care of patients with MPS IVA, appropriately integrating pharmacologic and surgical options |
|
|
|
|
|