Evaluation
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Very PoorPoorNeutralGoodExcellent
Overall Evaluation
Content
Usefulness
Quality
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(1=Strongly Disagree, 5= Strongly Agree)
12345
Review the diagnostic characteristics and updated treatment guidelines for MPS IVA/Morquio A syndrome
Examine pharmacologic therapeutic options for MPS IVA/MorquioA syndrome, and associated efficacy and safety data, including enzyme replacement therapeutics (ERTs)
Analyze available surgical options in the treatment of MPS IVA/Morquio A, as well as methods to minimize safety risks in the case of surgical complications
Develop and implement individualized treatment plans into the care of patients with MPS IVA, appropriately integrating pharmacologic and surgical options
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(1=NOT at all confident, 2=Somewhat confident, 3=Confident, 4=Very confident, 5=EXTREMELY confident, N/A=Not within the scope of my practice)
12345N/A
Apply the most current safety and efficacy data for emerging therapeutics to patients with Morquio A syndrome?
Create individualized Morquio A treatment plans to improve patient outcomes?
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(1=Never, 2=Not often, 3=Sometimes, 4=Often, 5=Always, N/A=Not applicable to me)
12345N/A
Evaluate urine KS measurements
Consider patients with short stature and joint hypermobility for Morquio A diagnosis
Provide annual pulmonary function screening to patients with Morquio A syndrome